Our Technology

Precision editing, redefined by Neoclease

Made possible by generative AI, our technology is more than a tool, it's the mechanism for treating genetic diseases. Our NeoMini editors are half the size of current industry editors, allowing for better delivery and packaging options.

The Platform

A closed-loop engine for engineering genome editors.

Better specificity Enhanced efficacy Targeted editing
Closed loop Closed-loop editor discovery design, simulate, validate, test, learn.
STEP 1 Generative design STEP 2 Viability gate STEP 3 Domain analysis STEP 4 MD simulation STEP 5 Validation STEP 6 Ranking STEP 7 Wet-lab → learn
Neoclease editor structure

Proprietary end-to-end. Every step runs on Neoclease's own models and scripts and writes structured data into a shared training set, so high-throughput analysis continually informs the model for more precise generation.

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How it works

  • Input: a target gene or disease-relevant site.
  • Model: our proprietary generative algorithm.
  • Validation: custom computational checks and gates.
  • Output: a custom-designed enzyme.
Generative AI

AI as a platform for gene editing.

Our secret weapon is a proprietary algorithm trained on all known nucleases, built on state-of-the-art neural network architectures. It acts like a compass, guiding us toward the design most likely to work for a given target, rather than starting from scratch each time.

Differentiation

Why not just use a standard Cas9 editor?

Neoclease takes a "lock and key" approach instead: an editor built fit-for-purpose for each target, so specificity, tissue reach, and immune profile are designed in from the start, not worked around afterward.

Fit for purpose

Every editor is designed for a single target

634aa
Compact class
non-NGG
PAM reach

A larger accessible genome

Miniature editors reach more of the genome

6,000+
Monogenic disorders in reach

Libraries, not one enzyme

Compact neuron-ready libraries

623–659aa
Compact class range
~10.8%
Identity to SpCas9
Lead Program

From platform to first program.

Here's where our lead program sits today.

Stage 1

Discovery

AI-guided design & early wet-lab validation

Stage 2

Preclinical

In vivo & safety studies

Stage 3

IND Filing

Regulatory submission

Stage 4

Phase 1

First-in-human trial

LRRK2
Parkinson's
Lead Program · Preclinical Stage

LRRK2-targeted editor for Parkinson's disease

Our first nuclease targets LRRK2, a gene strongly implicated in ~30% of Parkinson's disease. Our goal is a precise edit to slow or halt disease progression with a single dose. Our editor is small enough to deliver to the brain, reaching the cells that matter where other editors and drugs struggle to at meaningful levels.

The Foundation

Why synthetic biology matters.

Synthetic biology is the art and science of redesigning life at the molecular level, enabling tunable biology.

It's the foundation under everything above, the reason our editors can be both precise and effective, because every design decision traces back to the biology of the target itself.

Target gene Custom nuclease

Have a target in mind?

If you're a physician or scientist who's identified a gene standing between a patient and treatment, propose it as our next target.